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Vision and Focus

Our Vision is to discover, develop and deliver molecular medicines to treat and prevent diseases with significant unmet medical need.  We achieve this vision by focusing on significant product development opportunities that leverage our extensive capabilities in the development, manufacturing and commercialization of molecular medicines.

Our focused approach to business is to:

  • pursue development of our lead product candidates to treat inflammatory arthritis and eye disease
  • deliver on existing partnerships focused on HIV/AIDS vaccines and congestive heart failure
  • pursue additional product initiatives, particularly opportunities to exploit our leading IP position in expressed RNAi
  • leverage our investment in AAV manufacturing into additional strategic manufacturing relationships
  • manage our cash position and extend our horizon through equity raises, partnerships and grants

 

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